Association Française Niemann Pick
Por um escritor misterioso
Descrição
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Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A
Justin Hopkin - Board Member - Uplifting Athletes
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Niemann–Pick C disease: functional characterization of three NPC2 mutations and clinical and molecular update on patients with NPC2 - Verot - 2007 - Clinical Genetics - Wiley Online Library
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Maladie Niemann-Pick C - Journée d'info avec le soutien de Groupama RAA
Association Française Niemann Pick
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Advocacy – NNPDF
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Niemann-Pick disease type C: Members
Justin Hopkin - Board Member - Uplifting Athletes
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list of EURORDIS Member Associations.
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Correction of Deficient CD34+ Cells from Peripheral Blood after Mobilization in a Patient with Congenital Erythropoietic Porphyria: Molecular Therapy
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Defective Schwann cell lipid metabolism alters plasma membrane dynamics in Charcot-Marie-Tooth disease 1A
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Cyclophosphamide hydrate (Cyclophosphamide monohydrate), Alkylating Agent
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Delivery is key: lessons learnt from developing splice‐switching antisense therapies – topic of research paper in Nano-technology. Download scholarly article PDF and read for free on CyberLeninka open science hub.
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RareMD - Rare Disease Organizations
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por adulto (o preço varia de acordo com o tamanho do grupo)