Marta, with Niemann Pick C, fights for a cure with gene therapy
Por um escritor misterioso
Descrição
Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease
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Transmission Dynamics of a Mycobacterium tuberculosis Complex
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Selected Abstracts from the 12th Annual Meeting of the Clinical
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A new experimental model to promote research on the neurological
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From Life-Changing Clinical Trials to Running for Rare: Justin's
The development of gene therapy for Niemann-Pick Type C disease
![Marta, with Niemann Pick C, fights for a cure with gene therapy](https://rarediseases.org/wp-content/uploads/2022/06/nyc-5.jpg)
Voices of Rare Cancer: Jan's Story - National Organization for
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State of the Science - Beyond Batten Disease Foundation
![Marta, with Niemann Pick C, fights for a cure with gene therapy](https://www.biorxiv.org/content/biorxiv/early/2022/02/24/2022.02.21.479058/F2.large.jpg)
mRNA Treatment Rescues Niemann-Pick Disease Type C1 in Patient
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Startup Focused on Brain Cancer Treatment Wins $2,000 at Seed
![Marta, with Niemann Pick C, fights for a cure with gene therapy](https://www.yumpu.com/en/image/facebook/4627552.jpg)
F R I D A Y • A P R I L - Pediatric Academic Societies
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New Patient Journey Infographic Gives A Glimpse Into The
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Haematologica, Volume 107, Issue 6 by Haematologica - Issuu
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2017 ACVIM Forum Research Report Program - 2017 - Journal of
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Gene Therapy & Molecular Biology Volume 11 Issue A by Niko
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Marta – Columbus Children's Foundation
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por adulto (o preço varia de acordo com o tamanho do grupo)